Druggio

Congenital disorder of metabolism; Lysosomal storage disease

Diseases relevant to Congenital disorder of metabolism; Lysosomal storage disease

Gaucher disease

Treated by

Treated by

Niemann-Pick disease type C

Treated by

Mucopolysaccharidosis type I, Hurler-Scheie syndrome, Hurler syndrome, Scheie syndrome

Treated by

Mucopolysaccharidosis type II, Hunter syndrome

Treated by

イズカーゴ Hunterase Elaprase

Mucopolysaccharidosis type IV

Treated by

Mucopolysaccharidosis type VI, Maroteaux-Lamy syndrome

Treated by

Lysosomal acid lipase deficiency

Treated by